# Gene Therapy & Rare Diseases with Assoc. Prof Leszek Lisowski (449)

An episode of [Shirtloads of Science](https://invisiblenetwork.ai/podcast/1167803730), 25 Oct 2025, 33 min.

Audio: https://traffic.libsyn.com/secure/shirtloadsofscience/SOS_449_LL_Rare_Genetic_Diseases.mp3?dest-id=436327

In this episode, we speak with Associate Professor Leszek Lisowski, Head of the Translational Vectorology Unit at the Children's Medical Research Institute (CMRI), about the cutting-edge world of gene therapy. He explains how viral vectors are engineered to deliver life-saving treatments for rare genetic diseases - many of which are so uncommon, they're only known by the name of the affected gene. Despite being often overlooked, genetic diseases impact 10% of adults and 30% of children in hospitals. Leszek sheds light on the challenges of diagnosis, the promise of emerging genetic testing, and how his work is paving the way for more accurate, effective therapies. Linkedin: Children's Medical Research Institute, Leszek Lisowski Facebook: @jeansforgenes Instagram: @jeansforgenesau

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